Gene Therapy Contents: Volume 29 Number 5

In this Issue: Review Article Article Brief Communication Correction

Gene Therapy Contents: Volume 29 Issue 5

Review Article

Genome editing using CRISPR/Cas9 to treat hereditary hematological disorders Yan Chen, Ruiting Wen, Zhigang Yang & Zhanghui Chen Review Article | 09 March 2021 Gene Therapy 29 | doi:10.1038/s41434-021-00247-9

Article

Overexpression of miR-144-3p alleviates polycystic ovaries syndrome through targeting expression of HSP-70 Bing Qu, Qinghong Zhao, Qinglian Ma, Tian Yang, Xueyao Li et al. Article | 11 September 2020 Gene Therapy 29 | doi:10.1038/s41434-020-00191-0

Ectopic expression of BBS1 rescues male infertility, but not retinal degeneration, in a BBS1 mouse model Matthew R. Cring, Kacie J. Meyer, Charles C. Searby, Adam Hedberg-Buenz, Michael Cave et al. Article | 04 March 2021 Gene Therapy 29 | doi:10.1038/s41434-021-00241-1

Screening for gene doping transgenes in horses via the use of massively parallel sequencing Jillian Maniego, Bogusia Pesko, Jocelyn Habershon-Butcher, Jim Huggett, Polly Taylor et al. Article | 19 July 2021 Gene Therapy 29 | doi:10.1038/s41434-021-00279-1

Thrombopoietin-based CAR-T cells demonstrate in vitro and in vivo cytotoxicity to MPL positive acute myelogenous leukemia and hematopoietic stem cells Jaquelyn T. Zoine, Chengyu Prince, Jamie Y. Story, Gianna M. Branella, Allison M. Lytle et al. Article | 13 August 2021 Gene Therapy 29 | doi:10.1038/s41434-021-00283-5

Development and biological characterization of a clinical gene transfer vector for the treatment of MAK-associated retinitis pigmentosa Budd A. Tucker, Erin R. Burnight, Cathryn M. Cranston, Mallory J. Ulferts, Meagan A. Luse et al. Article | 14 September 2021 Gene Therapy 29 | doi:10.1038/s41434-021-00291-5

Long-term safety and efficacy of intramyocardial adenovirus-mediated VEGF-DΔNΔC gene therapy eight-year follow-up of phase I KAT301 study Aleksi J. Leikas, Iiro Hassinen, Antti Hedman, Antti Kivelä, Seppo Ylä-Herttuala et al. Article | 01 October 2021 Gene Therapy 29 | doi:10.1038/s41434-021-00295-1

Epigenetic repression of gonadotropin gene expression via a GnRH-mediated DNA delivery system Lilach Pnueli & Philippa Melamed Article | 17 March 2022 Gene Therapy 29 | doi:10.1038/s41434-022-00325-6

Brief Communication

Molecular targeting of vulnerable RNA sequences in SARS CoV-2: identifying clinical feasibility G. Ian Gallicano, John L. Casey, Jiayu Fu & Samiksha Mahapatra Brief Communication | 12 November 2020 Gene Therapy 29 | doi:10.1038/s41434-020-00210-0

Correction

Correction: Maximizing lentiviral vector gene transfer in the CNS Morgane Humbel, Mergim Ramosaj, Virginie Zimmer, Sara Regio, Ludiwine Aeby et al. Correction | 12 April 2022 Gene Therapy 29 | doi:10.1038/s41434-022-00334-5

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